For Avery and Addison, we go beyond every day

Advancing medicines for rare diseases

Learn more

Leading with purpose. Every day.

“Ultragenyx was founded to advance innovative medicines for rare and ultrarare diseases that have never been treated before. We are delivering transformative therapies across multiple indications, and we have one of the most robust and diverse clinical pipelines in rare disease. Our focus is on doing the right things for patients both during development and commercialization to deliver on the promise of these therapies in a way that's meaningful for rare disease communities.”

Emil D. Kakkis, M.D., Ph.D.
Chief Executive Officer and President

Leadership

Leadership Home

Our team of passionate biopharmaceutical leaders combines deep expertise in drug development and commercialization

Meet our leadership team

Pipeline

Pipeline Card

We have one of the largest and most diverse pipelines in rare disease

Explore our pipeline

Careers

Careers Card

Join our talented team

Browse current opportunities
February 27, 2024

Ultragenyx to Participate at Investor Conferences in March

Read press release
February 23, 2024

Ultragenyx Reports Inducement Grant Under Nasdaq Listing Rule 5635(c)(4)

Read press release
February 15, 2024

Ultragenyx Reports Fourth Quarter and Full Year 2023 Financial Results and Corporate Update

Read press release
Rare Perspective Home

Rare perspective

Insights and information on our approach to collaborating with rare disease communities, supporting our teammates at Ultragenyx, and developing new therapies for rare disease

Read our blog >